SOUTH PLAINFIELD, N.J. and
SAN RAFAEL, Calif., June 12, 2015 /PRNewswire/ -- PTC
Therapeutics, Inc. (NASDAQ: PTCT) and BioMarin Pharmaceutical Inc.
(NASDAQ: BMRN) announced today that they will host an Industry
Update Symposium on Advances in Duchenne Muscular Dystrophy (DMD)
and Biomarkers on Monday, June
22nd from 10 am –
1 pm ET at the Le Parker Meridien in
New York City. Leading experts in
the field will review the latest research on DMD, including natural
history data, clinical biomarkers, and imaging assessments used in
monitoring disease progression and response to therapy. An overview
of state-of-the-art therapies in development for DMD will be
discussed.
A live webcast of the event will be available on the Events and
Presentations page under the investor relations section of PTC
Therapeutics' and BioMarin's websites at www.ptcbio.com and at
www.BMRN.com. A replay of the presentation will be archived. The
presentation will be archived for 2 weeks following the
presentation. It is recommended that users connect to the company
website several minutes prior to the start of the webcast to ensure
a timely connection.
About PTC Therapeutics, Inc.
PTC is a global
biopharmaceutical company focused on the discovery, development and
commercialization of orally administered, proprietary small
molecule drugs targeting an area of RNA biology we refer to as
post-transcriptional control. Post-transcriptional control
processes are the regulatory events that occur in cells during and
after a messenger RNA is copied from DNA through the transcription
process. PTC's internally discovered pipeline addresses multiple
therapeutic areas, including rare disorders, oncology and
infectious diseases. PTC has discovered all of its compounds
currently under development using its proprietary technologies. PTC
plans to continue to develop these compounds both on its own and
through selective collaboration arrangements with leading
pharmaceutical and biotechnology companies. For more information on
the company, please visit our website www.ptcbio.com.
About BioMarin
BioMarin develops and commercializes innovative biopharmaceuticals
for serious diseases and medical conditions. The company's product
portfolio comprises five approved products and multiple clinical
and pre-clinical product candidates. Approved products include
Vimizim® (elosulfase alfa) for MPS IVA, a product wholly developed
and commercialized by BioMarin; Naglazyme® (galsulfase) for MPS VI,
a product wholly developed and commercialized by BioMarin;
Aldurazyme® (laronidase) for MPS I, a product which BioMarin
developed through a 50/50 joint venture with Genzyme Corporation;
Kuvan® (sapropterin dihydrochloride) Powder for Oral Solution and
Tablets, for phenylketonuria (PKU), developed in partnership with
Merck Serono, a division of Merck KGaA of Darmstadt, Germany and Firdapse® (amifampridine), which
has been approved by the European Commission for the treatment of
Lambert Eaton Myasthenic Syndrome (LEMS). Product candidates
include drisapersen, an exon skipping oligonucleotide, for which a
marketing application has been submitted to FDA and EMA for the
treatment of patients with Duchenne muscular dystrophy (DMD) with
mutations in the dystrophin gene that are amenable to treatment
with exon 51 skipping, pegvaliase (PEGylated recombinant
phenylalanine ammonia lyase, formerly referred to as BMN 165 or
PEG PAL), which is currently in
Phase 3 clinical development for the treatment of PKU, talazoparib
(formerly referred to as BMN 673), a poly ADP-ribose polymerase
(PARP) inhibitor, which is currently in Phase 3 clinical
development for the treatment of germline BRCA breast cancer,
reveglucosidase alfa (formerly referred to as BMN 701), a novel
fusion protein of insulin-like growth factor 2 and acid alpha
glucosidase (IGF2-GAA), which is currently in Phase 3 clinical
development for the treatment of Pompe disease, BMN 111, a modified
C-natriuretic peptide, which is currently in Phase 2 clinical
development for the treatment of achondroplasia, BMN 044, BMN 045
and BMN 053, exon skipping oligonucleotides, which are currently in
Phase 2 clinical development for the treatment of Duchenne muscular
dystrophy (exons 44, 45 and 53), cerliponase alfa (formerly
referred to as BMN 190), a recombinant human tripeptidyl
peptidase-1 (rhTPP1) for the treatment of CLN2 disorder, a form of
Batten disease, which is currently in Phase 1, BMN 270, an
AAV-factor VIII vector, for the treatment of hemophilia A and BMN
250, a novel fusion of alpha-N-acetyglucosaminidase (NAGLU) with a
peptide derived from insulin-like growth factor 2 (IGF2), for the
treatment of MPS IIIB.
For additional information, please visit www.BMRN.com.
Information on BioMarin's website is not incorporated by reference
into this press release.
For More
Information:
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PTC
Therapeutics
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BioMarin
Pharmaceutical Inc.
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Investors:
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Emily
Hill
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Traci
McCarty
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+1(908)
912-9327
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(415)
455-7558
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ehill@ptcbio.com
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Media:
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Jane Baj
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Debra
Charlesworth
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+1 (908)
912-9167
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(415)
455-7451
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jbaj@ptcbio.com
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To view the original version on PR Newswire,
visit:http://www.prnewswire.com/news-releases/ptc-therapeutics-and-biomarin-pharmaceutical-to-host-dmd-industry-symposium-300098347.html
SOURCE PTC Therapeutics, Inc.